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The last 5 uploaded publications
Gene-corrected human iPSC-derived cardiomyocytes and skeletal muscles reveal partial dystrophin Dp427 preservation and cardiac Dp116 expression in Duchenne muscular dystrophy
Marta Białobrzeska, Marta Białobrzeska, Marta Przymuszała, Marta Przymuszała, Anna Kostera‐Pruszczyk, Urszula Florczyk, Jozef Dulak (2025). Gene-corrected human iPSC-derived cardiomyocytes and skeletal muscles reveal partial dystrophin Dp427 preservation and cardiac Dp116 expression in Duchenne muscular dystrophy. , DOI: https://doi.org/10.1101/2025.07.11.25331067.
Preprint49 days agoLack of miR-378 attenuates muscular dystrophy in mdx mice
Paulina Podkalicka, Olga Mucha, Iwona Bronisz-Budzyńska, Magdalena Kozakowska, Katarzyna Pietraszek‐Gremplewicz, Anna Cetnarowska, Urszula Głowniak-Kwitek, Karolina Bukowska-Straková, Maciej Cieśla, Maria Kulecka, Jerzy Ostrowski, Michał Mikuła, Anna Potulska‐Chromik, Anna Kostera‐Pruszczyk, Alicja Józkowicz, Agnieszka Łoboda, Jozef Dulak (2020). Lack of miR-378 attenuates muscular dystrophy in mdx mice. , 5(11), DOI: https://doi.org/10.1172/jci.insight.135576.
Article49 days agoHeme Oxygenase-1 Influences Satellite Cells and Progression of Duchenne Muscular Dystrophy in Mice
Urszula Glowniak, Krzysztof Szade, Jacek Stępniewski, Mateusz Jeż, Kalina Andrysiak, Karolina Bukowska-Straková, Anna Kamińska, Anna Kostera‐Pruszczyk, Alicja Józkowicz, Agnieszka Łoboda, Jozef Dulak, Katarzyna Pietraszek‐Gremplewicz, Magdalena Kozakowska, Iwona Bronisz-Budzyńska, Maciej Cieśla, Olga Mucha, Paulina Podkalicka, Magdalena Madej (2018). Heme Oxygenase-1 Influences Satellite Cells and Progression of Duchenne Muscular Dystrophy in Mice. , 29(2), DOI: https://doi.org/10.1089/ars.2017.7435.
Article49 days agoDysregulated iron homeostasis in dystrophin-deficient cardiomyocytes: correction by gene editing and pharmacological treatment
Kalina Andrysiak, Gabriela Machaj, Dominik Priesmann, Olga Woźnicka, Alicja Martyniak, Guillem Ylla, Marcus Krüger, Elżbieta Pyza, Anna Potulska‐Chromik, Anna Kostera‐Pruszczyk, Agnieszka Łoboda, Jacek Stępniewski, Jozef Dulak (2023). Dysregulated iron homeostasis in dystrophin-deficient cardiomyocytes: correction by gene editing and pharmacological treatment. , 120(1), DOI: https://doi.org/10.1093/cvr/cvad182.
Article49 days agoGeneration of DMBi002-A human induced pluripotent stem cell line from patient with Spinal muscular atrophy type 3
Kalina Andrysiak, Alicja Martyniak, Anna Potulska‐Chromik, Anna Kostera‐Pruszczyk, Jacek Stępniewski, Jozef Dulak (2021). Generation of DMBi002-A human induced pluripotent stem cell line from patient with Spinal muscular atrophy type 3. , 57, DOI: https://doi.org/10.1016/j.scr.2021.102563.
Article49 days ago