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The last 5 uploaded publications
Gene-corrected human iPSC-derived cardiomyocytes and skeletal muscles reveal partial dystrophin Dp427 preservation and cardiac Dp116 expression in Duchenne muscular dystrophy
Marta Białobrzeska, Marta Białobrzeska, Marta Przymuszała, Marta Przymuszała, Anna Kostera‐Pruszczyk, Urszula Florczyk, Jozef Dulak (2025). Gene-corrected human iPSC-derived cardiomyocytes and skeletal muscles reveal partial dystrophin Dp427 preservation and cardiac Dp116 expression in Duchenne muscular dystrophy. , DOI: https://doi.org/10.1101/2025.07.11.25331067.
Preprint8 days agoGene-corrected human iPSC-derived cardiomyocytes and skeletal muscles reveal partial dystrophin Dp427 preservation and cardiac Dp116 expression in Duchenne muscular dystrophy
Marta Białobrzeska, Marta Białobrzeska, Marta Przymuszała, Marta Przymuszała, Anna Kostera‐Pruszczyk, Urszula Florczyk, Jozef Dulak (2025). Gene-corrected human iPSC-derived cardiomyocytes and skeletal muscles reveal partial dystrophin Dp427 preservation and cardiac Dp116 expression in Duchenne muscular dystrophy. , DOI: https://doi.org/10.1101/2025.07.11.25331067.
Preprint8 days agoGeneration of human induced pluripotent stem cell line derived from Becker muscular dystrophy patient with CRISPR/Cas9-mediated correction of DMD gene mutation
Marta Przymuszała, Alicja Martyniak, J Kwiatkowska, Jarosław Meyer-Szary, Karolina Śledzińska, Jolanta Wierzba, Jozef Dulak, Urszula Florczyk, Jacek Stępniewski (2024). Generation of human induced pluripotent stem cell line derived from Becker muscular dystrophy patient with CRISPR/Cas9-mediated correction of DMD gene mutation. , 76, DOI: https://doi.org/10.1016/j.scr.2024.103327.
Article8 days ago274P Generation of cardiac organoids from DuchenneMuscularDystrophy patient-derived induced pluripotent stem cells: a novel approach to understanding cardiomyopathy
Marta Przymuszała, Jacek Stępniewski, Urszula Florczyk, Jozef Dulak (2024). 274P Generation of cardiac organoids from DuchenneMuscularDystrophy patient-derived induced pluripotent stem cells: a novel approach to understanding cardiomyopathy. , 43, DOI: https://doi.org/10.1016/j.nmd.2024.07.092.
Article8 days ago